lymphoblastic leukaemia

World-first base-edited gene therapy helps patients fight previously incurable blood cancer

Posted in Highlights from UCL, Medicine, Science on 17th Dec, 2025
by Alexander Muller

A groundbreaking new treatment using genome-edited immune cells, developed by scientists at UCL and Great Ormond Street Hospital (GOSH), has shown promising results in helping children and adults fight a rare and aggressive form of blood cancer.