gene therapy

CRISPR enters its first human clinical trials

Posted in Medicine, Science on 18th Aug, 2019
by Alex Muller

In the first spate of clinical trials, scientists are using CRISPR/Cas9 to combat cancer and blood disorders in people.

Breakthrough crispr gene editing trial set to begin this year

Posted in Science on 17th Apr, 2018
by Alex Muller

Biotech company CRISPR Therapeutics is set to treat Europes patients with the CRISPR gene-editing tool this year following regulatory approval for trials.

Gene therapy infused into persons blood to correct liver enzymes

Posted in Science on 17th Nov, 2017
by Alex Muller

When the enzyme is defective or missing, the sugars build up and can cause developmental delays, organ problems, brain damage, and early death.

Scientists develop gene therapy that could restore partial vision

Posted in Science on 13th Nov, 2017
by Alex Muller

The new gene therapy is under review by the US Food and Drug Administration.

Teenager's sickle cell reversed with world-first therapy

Posted in Medicine on 3rd Mar, 2017
by Alex Muller

A French teenager's sickle cell disease has been reversed using a pioneering treatment to change his DNA.